Clinical Trials Overview

A key goal of the DuchenneConnect registry is to assist in developing new clinical treatment trials and other research studies for Duchenne/Becker muscular dystrophy. We hope to achieve this goal by connecting the medical research communities and families affected by Duchenne to enable the flow of information between them.

The topic areas under the Clinical Trials Menu provide information about the goals and process of clinical treatment trials and answer frequently asked questions about participating in research opportunities. We encourage you to explore the main areas of the clinical trials section.

Using the DuchenneConnect Registry to Recruit for Clinical Trials offers information for study investigators, sponsors, and research professionals who wish to partner with DuchenneConnect to identify potential candidate participants for clinical treatment trials and other research studies. Other DuchenneConnect members may also find this section helpful in understanding how the selection and recruitment process works.

All registered DuchenneConnect participants — Duchenne families and providers — are eligible to receive notification of research studies, including recruitment, updates and results outcomes.