Direct Access Webinars

DuchenneConnect and Parent Project Muscular Dystrophy present a webinar series that allows you direct access to experts in the fight to end Duchenne. Whether it's a researcher offering updates on a developing therapy, or industry providing clinical trial information, or experts in care and management, this series will be your resource to find out what is going on in the community from the people making it happen. Please contact us at This email address is being protected from spambots. You need JavaScript enabled to view it. if you have questions about recent webinars or recommendations for upcoming webinars.

Webinar Archive

January 24, 2018

Givinostat Update from Italfarmaco 

Speaker:  Dr. Paolo Bettica, VP R&D - Italfarmaco

December 15, 2017

Understanding Gene Therapy, Part 3:  Galgt2 and Dup2

Speaker:  Dr. Kevin Flanigan - Nationwide Children's Hospital

November 30, 2017

Capricor Therapeutics' HOPE-Duchenne Clinical Trial

Speakers: Linda Marban, CEO - Capricor;  Dr. Ron Victor - Cedars Sinai Heart Institute

November 14, 2017

WAVE Life Sciences Webinar

Speakers:  Drs. Michael Panzara and Matthew Wood;  Wendy Erler 

October 25, 2017

Update on FibroGen's Development of Pamrevlumab

Speaker:  FibroGen team

October 11, 2017

MoveDMD Open Label Extension Webinar

Speaker:  Joanne Donovan, MD, PhD, Chief Medical Officer - Catabasis

September 6, 2017

Gene Therapy for Duchenne at Nationwide Children's Hospital, Part 2

Speaker:  Jerry Mendell, MD - Nationwide Children's Hospital

August 9, 2017

Understanding Gene Therapies for Duchenne, Part 1

Speakers: Melissa Spencer, PhD - UCLA and Lee Sweeney, PhD - University of Florida

June 7, 2017

Saprepta's ESSENCE Clinical Trial for Exon 45 & 53 Skipping

Speaker: Dr. Genevieve Laforet, Medical Director - Sarepta

May 17, 2017

Nationwide Children's Hospital Carrier Study

Speakers: Dr. Kan Hor and Dr. May Ling Mah - Nationwide Children's Hospital

April 26, 2017

Givinostat: An HDAC Inhibitor in Development for the Treatment of Duchenne

Speaker:  Dr. Paolo Bettica, VP of R&D - Italfarmaco

March 27, 2017

Akashi Therapeutics:  Update on HT-100

Speaker:  Dr. Marc Blaustein, CEO - Akashi

March 9, 2017

Santhera:  Idebenone and the SIDEROS Trial

Speakers:  Dr. Thomas Meier and Jodi Wolff, PhD, Santhera Pharmaceuticals

February 22, 2017

Updates on NS Pharma's Exon 53 Skipping Trial

Speakers:  Dr. Paula Clemens and Lauren Morgenroth, CINRG

February 2, 2017

Updates on MoveDMD Trial from Catabasis

Speaker:  Dr. Joanne Donovan, CMO - Catabasis

February 1, 2017

MissionDMD: FibroGen's AntiFibrosis Program

Speaker:  Ewa Glossary Link Carrier, MD - FibroGen

January 25, 2017

Summit's Utrophin Modulation: A Universal Treatment Approach to DMD

Speakers:  Jon Tinsley (CSO) and Ralf Rosskamp (CMO) - Summit Therapeutics

January 18, 2017

Vamorolone (VBP15) Clinical Trials in Duchenne

Speaker:  Dr. Eric Hoffman, CEO - ReveraGen BioPharma

December 15, 2016

A Closer Look at the Potential of CRISPR/Cas9 in Duchenne

Speaker:  Dr. Eric Olson, UT Southwestern Medical Center

November 16, 2016 

NS Pharma's Exon 53 Skipping Program

Speakers:  Dr. Paula Clemens and Lauren Morgenroth, CINRG

November 14, 2016

Deflazacort Access: Navigating Potential Changes to Your Prescription

Speakers:  Masters Pharmaceuticals

August 1, 2016

PTC Therapeutics:  Regulatory Update on Translarna

Speaker:  Dr. Craig McDonald, UC-Davis

July 13, 2016

What is CRISPR/Cas9?

Speaker:  Dr. Eric Olson, UT Southwestern Medical Center - Dallas

June 8, 2016

Catabasis Webinar on the MoveDMD Clinical Trial

Speaker:  Dr. Joanne Donovan, CMO, Catabasis Pharmaceuticals

May 18, 2016

FibroGen MissionDMD Webinar

Speakers: Pat Furlong, CEO, PPMD and Ewa Carrier, MD, FibroGen

March 30, 2016

BMS Anti-Myostatin Adnectin Webinar

Speaker:  Leslie Jacobsen, MD, Bristol-Myers Squibb

January 13, 2016

HOPE-Duchenne Trial - Capricor Therapeutics

Speakers:  Deborah Ascheim, MD & CMO, and Linda Marban, PhD & CEO, Capricor Therapeutics

Webinar Archive